You have 9 free searches left this month | for more free features.
Clincosm LogoSign in Get a demo

Splicing Modulator

Showing 1 - 25 of 293
STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS
LAST UPDATED

Leukemia, Myeloid, Acute, MDS, Leukemia, Myelomonocytic, Chronic Trial in Worldwide (H3B-8800 (RVT-2001))

Recruiting
  • Leukemia, Myeloid, Acute
  • +2 more
  • H3B-8800 (RVT-2001)
  • Stanford, California
  • +26 more
Mar 23, 2022

Cystic Fibrosis, CFTR Gene Mutation Trial in Montpellier (Nasal cells sampling, Rectal biopsy sampling)

Recruiting
  • Cystic Fibrosis
  • CFTR Gene Mutation
  • Nasal cells sampling
  • Rectal biopsy sampling
  • Montpellier, France
    Montpellier University Hospital
Mar 31, 2022

Development of Targeted RNA-Seq for Amyotrophic Lateral

Not yet recruiting
  • Amyotrophic Lateral Sclerosis
  • RNA sequencing
  • Bordeaux, France
  • +6 more
Oct 9, 2023

Spinal Muscular Atrophy Trial in Worldwide (Risdiplam)

Active, not recruiting
  • Spinal Muscular Atrophy
  • Palo Alto, California
  • +23 more
Jan 19, 2023

Effectiveness of CFTR Modulators According to Co-therapy

Not yet recruiting
  • Cystic Fibrosis
  • Discontinuation of respiratory co-therapy (azithromycin, RhDNase, or inhaled antibiotics)
  • (no location specified)
Dec 15, 2022

Healthy Trial in Merksem (Adalimumab, Lipopolysaccharide (LPS))

Recruiting
  • Healthy
  • Merksem, Belgium
    Clinical Pharmacology Unit
May 22, 2023

Atypical Hemolytic Uremic Syndrome, Membranoproliferative Glomerulonephritis, Autosomal Dominant Polycystic Kidney Trial in

Not yet recruiting
  • Atypical Hemolytic Uremic Syndrome
  • +3 more
  • Skin biopsy
  • Ranica, BG, Italy
    Centro di Ricerche Cliniche per le Malattie Rare "Aldo e Cele Da
Aug 9, 2023

SMN Circular RNAs as Potential New Targets and Biomarkers for

Recruiting
  • Spinal Muscular Atrophy
    • Rome, Italy
      Policlinico gemelli
    Feb 27, 2023

    Longitudinal Effects of CFTR Modulator Drugs

    Active, not recruiting
    • Cystic Fibrosis
      • Denver, Colorado
        National Jewish Health
      Sep 28, 2022

      Anti-platelet Drug Exposure on Platelet mRNA Splicing in Healthy

      Withdrawn
      • Thrombosis; Artery
      • Ticagrelor Oral Tablet [Brilinta]
      • Washington, District of Columbia
      • +1 more
      Oct 21, 2021

      Taybi Linder Syndrome, Microcephalic Osteodysplastic Primordial Dwarfism Types I and III, Roifman Syndrome Trial in France

      Not yet recruiting
      • Taybi Linder Syndrome
      • +3 more
      • Blood samples
      • +2 more
      • Bordeaux, France
      • +5 more
      Oct 26, 2023

      Acute Myeloid Leukemia, MDS, Chronic Myelomonocytic Leukemia Trial in United States (E7820)

      Recruiting
      • Acute Myeloid Leukemia
      • +2 more
      • Miami, Florida
      • +6 more
      Apr 25, 2022

      CFTR Modulators in Pregnant Individuals and in Postpartum

      Not yet recruiting
      • Cystic Fibrosis
      • Pregnancy
        • Minneapolis, Minnesota
          University of Minnesota
        Jan 6, 2023

        Neurodegeneration in Multiple Sclerosis -Preclinical Study

        Not yet recruiting
        • Relapsing-Remitting Multiple Sclerosis (RRMS)
        • +2 more
        • Peripheral blood withdrawal
        • Pozzilli, Isernia, Italy
        • +2 more
        Feb 15, 2022

        Cystic Fibrosis Trial in Baltimore (VX-522)

        Recruiting
        • Cystic Fibrosis
        • VX-522
        • Baltimore, Maryland
          Baltimore - Early Phase Clinical Unit
        Jan 4, 2023

        ive Modulator Therapy on the Cystic Fibrosis Microbiome

        Not yet recruiting
        • Cystic Fibrosis
        • Nasal endoscopy with microbiome swab and mucus collection through filter paper and sponge
        • +2 more
        • (no location specified)
        Aug 1, 2023

        Alcohol Use Disorder Trial in New York (CI-581a, CI-581b, MBRP)

        Recruiting
        • Alcohol Use Disorder
        • New York, New York
          NYSPI
        Mar 29, 2022

        Cystic Fibrosis Lung Trial in United States (4D-710)

        Recruiting
        • Cystic Fibrosis Lung
        • 4D-710
        • Denver, Colorado
        • +5 more
        Jul 14, 2022

        Alcohol Drinking, Alcohol-Related Disorders, Disease Trial in Catonsville (Minocycline, Sugar pill)

        Recruiting
        • Alcohol Drinking
        • +15 more
        • Catonsville, Maryland
          Maryland Psychiatric Research Center (MPRC) Treatment Research P
        Nov 29, 2022

        Breast Cancer, Early-stage Breast Cancer, High Risk Breast Carcinoma Trial in United States (Abemaciclib, Tamoxifen,

        Not yet recruiting
        • Breast Cancer
        • +2 more
        • Boston, Massachusetts
        • +7 more
        Aug 14, 2023

        Sweat Chloride and Their Association With Clinical Outcomes

        Active, not recruiting
        • Cystic Fibrosis
          • Birmingham, Alabama
          • +51 more
          Jun 16, 2022

          Intracerebral Hemorrhage Trial (Fingolimod)

          Not yet recruiting
          • Intracerebral Hemorrhage
          • (no location specified)
          Oct 17, 2023

          Post-acute Sequelae of COVID-19, Depressive Symptoms, Cognitive Dysfunction Trial (CI-581a, CI-581b)

          Not yet recruiting
          • Post-acute Sequelae of COVID-19
          • +2 more
          • (no location specified)
          Jan 24, 2023

          Multiple Myeloma, Lymphoma, Large B-Cell, Diffuse, Pleiotropic Pathway Modifier Trial in Worldwide (CC-122)

          Active, not recruiting
          • Multiple Myeloma
          • +5 more
          • Duarte, California
          • +38 more
          Aug 18, 2022

          Effectiveness in Cystic Fibrosis

          Active, not recruiting
          • Cystic Fibrosis
          • Contraception
            • Birmingham, Alabama
            • +9 more
            May 11, 2022